참고문헌
- Dunbar CE (1996): Gene transfer to hematopoietic stem cells: implications for gene therapy of human disease. Annu Rev Med 47:11-20 https://doi.org/10.1146/annurev.med.47.1.11
- Ballas CB, Zielske SP, Gerson, SL (2002): Adult bone marrow stem cells for cell and gene therapies: implications for greater use. J Cell Biochem Suppl 38:20-28
- Engel BC, Kohn, DB (2003): Gene therapy for inborn and acquired immune deficiency disorders. Acta Haematol 110:60-70 https://doi.org/10.1159/000072455
- Cornetta K, Fan Y (1997): Retroviral gene therapy in hematopoietic diseases. J Clin Apheresis 12:187-193 https://doi.org/10.1002/(SICI)1098-1101(1997)12:4<187::AID-JCA6>3.0.CO;2-6
- Cavazzana CM, Hacein BS, Saint BG, Gross F, Yvon E, Nusbaum P, Selz F, Hue C, Certain S, Casanova JL, Bousso P, Deist FL, Fischer A (2000): Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease. Science 288: 669-672 https://doi.org/10.1126/science.288.5466.669
- Hacein BAS, Deist F, Carlier F, Bouneaud C, Hue C, Villartay JP, Thrasher AJ, Wulffraat N, Sorensen R, Dupuis GS, Fischer A, Davies EG, Kuis W, Leiva L, Cavazzana CM (2002): Sustained correction of Xlinked severe combined immunodeficiency by ex vivo gene therapy. N Engl J Med 346:1185-1193 https://doi.org/10.1056/NEJMoa012616
- Hanenberg H, Xiao XL, Dilloo D, Hashino K, Kato I, Williams DA (1996): Colocalization of retrovirus and target cells on specific fibronectin fragments increases genetic transduction of mammalian. Nat Med 2:876-882 https://doi.org/10.1038/nm0896-876
- Kurre P, Morris J, Horn PA, Harkey MA, Andrews RG, Kiem HP (1998): Improved gene transfer into baboon marrow repopulating cells using recombinant human fibronectin fragment CH-296 in combination with interleukin-6, stem cell factor, FLT-3 ligand, and megakaryocyte growth and development factor. Blood 92:1878-1886
- Abonour R (2000): Efficient retrovirus-mediated transfer of the multidrug resistance 1 gene into autologous human long term repopulating hematopoietic stem cells. Nat Med 6:652-658.10 https://doi.org/10.1038/76225
- Kohn DB, Sadelain M, Dunbar C, Bodine D, Kiem HP, Candotti F, Tisdale J, Riviere I, Blau CA, Richard RE, Sorrentino B, Nolta J, Malech H, Glorioso J (2003): American Society of Gene Therapy (ASGT) ad hoc subcommittee on retroviral-mediated gene transfer to hematopoietic stem cells. Mol Ther 8:180-187 https://doi.org/10.1016/S1525-0016(03)00212-0
- Rosenberg SA, Blaese RM, Brenner MK, Deisseroth AB, Ledley FD, Lotze MT, Wilson JM, Nabel GJ, Walker R (2000): Human gene marker/therapy clinical protocols. Hum Gene Ther 11:919-979 https://doi.org/10.1089/10430340050015536
- Wright DE, Wagers AJ, Gulati AP, Johnson FL, Weissman IL (2001): Physiological migration of hematopoietic stem and progenitor cells. Science 294:1933-1936 https://doi.org/10.1126/science.1064081
-
Wagers AJ, Allsopp RC, Weissman IL (2002): Changes in integrin expression are associated with altered homing properties of
$Lin^{-/low}Thy1.1^{low}Sca-1^-c-Kit^-$ -hematopoietic stem cells following mobilization by cyclophosphamide/granulocyte colony-stimulating factor. Exp Hematol 30:176-185 https://doi.org/10.1016/S0301-472X(01)00777-9 -
Jetmore A, Plett PA, Tong X (2002): Homing efficiency, cell cycle kinetics, and survival of quiescent and cycling human
$CD34^-$ cells transplanted into conditioned NOD/SCID recipients. Blood 99:1585-1593 https://doi.org/10.1182/blood.V99.5.1585 - Yahata T, Ando K, Sato T, Miyatake H, Nakamura Y, Muguruma Y, Kato S, Hotta T (2003): Ahighly sensitive strategy for SCID-repopulating cell assay by direct injection of primitive human hematopoietic cells into NOD/SCID mice bone marrow Blood 15:2905-2913
-
Burger JA, Spoo A, Dwenger A, Burger M, Behringer D (2003): CXCR4 chemokine receptors (CD184) and alpha4beta1 integrins mediate spontaneous migration of human
$CD34^+$ progenitors and acute myeloid leukaemia cells beneath marrow stromal cells (pseudoemperipolesis). Br J Haematol 122:579-89 https://doi.org/10.1046/j.1365-2141.2003.04466.x - Peters SO, Kittler ELW, Ramshaw HS, Quesenberry PJ (1995): Murine marrow cells expanded in culture with IL-3, IL-6, and SCF acquire an engraftment defect in normal hosts. Exp Hematol 23:461-469
- Szilvassy SJ, Bass MJ, Zant GV, Grimes B (1999) Organ selective homing defines engraftment kinetics of murine hematopoietic stem cells and is compromised by ex vivo expansion. Blood 93:1557-1566
- Onodera M, Yachie A, Nelson DM, Welchlin H, Morgan RA, Blaese RM (1997): A simple and reliable method for screening retroviral producer clones without selectable markers. Hum Gene Ther 8:1189-1194 https://doi.org/10.1089/hum.1997.8.10-1189
- Culver KW (1994): The first human gene therapy experiment. Gene therapy-A handbook for physician. Marry Ann Liebert 1:33-40
- Kaneko S, Onodera M, Fujiki Y, Nagasawa T, Nakauchi H (2001): Simplified retroviral vector GCsap with murine stem cell virus long terminal repeat allows high and continued expression of enhanced green fluorescent protein by human hematopoietic progenitors engrafted in NOD/SCID Mice. Human gene thrapy 12:35-44 https://doi.org/10.1089/104303401450942
- Worsham DN, Schuesler T, Kalle CV, Pan D (2006): In vivo gene transfer into adult stem cells in unconditioned mice by in situ delivery of a lentiviral vector. Mol Ther 14:514-524 https://doi.org/10.1016/j.ymthe.2006.05.014
- Kushida T, Inaba M, Hisha H (2001): Intra-bone marrow injection of allogeneic bone marrow cells: a powerful new strategy for treatment of intractable autoimmune diseases in MRL/lpr mice. Blood 97:3292-3299 https://doi.org/10.1182/blood.V97.10.3292
- Nelson DM, Metzger ME, Donahue RE, Morgan RA (1997): In vivo retrovirus mediated gene transfer into multiple hematopoietic lineages in rabbits without preconditioning. Hum Gene Therapy 8:747-754 https://doi.org/10.1089/hum.1997.8.6-747
- Porada CD, Tran ND, Zhao Y, Anderson WF, Zanjani ED (2000): Neonatal gene therapy: transfer and expression of exogenous genes in neonatal sheep following direct injection of retroviral vectors into the bone marrow space. Exp Hematol 28:642-650 https://doi.org/10.1016/S0301-472X(00)00158-2
- Pike-OK, Ridder D, Weerkamp F, Baert MR, Thrasher AJ, Wagemaker G, van Dongen JJ, Staal FJ (2006): Gene therapy: Is IL2RG oncogenic in T-cell development?. Nature 21:443-444