Journal of The Korean Society of Inherited Metabolic disease (대한유전성대사질환학회지)
- Volume 10 Issue 1
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- Pages.59-66
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- 2010
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- 2287-4712(pISSN)
Enzyme Replacement Therapy in Patients Who Have Mucopolysaccharidosis and Are younger than 5 years old
5세 미만 뮤코다당체침착증 환자에서의 효소 대체 요법
- Park, Seong-Won (Department of Pediatrics, Samsung Medical Center, Sungkyunkwan University School of Medicine) ;
- Son, Yeong-Bae (Department of Pediatrics, Samsung Medical Center, Sungkyunkwan University School of Medicine) ;
- Kim, Se-Hwa (Department of Pediatrics, Samsung Medical Center, Sungkyunkwan University School of Medicine) ;
- Jo, Seong-Yun (Department of Pediatrics, Samsung Medical Center, Sungkyunkwan University School of Medicine) ;
- Ji, Seon-Tae (Department of Pediatrics, Samsung Medical Center, Sungkyunkwan University School of Medicine) ;
- Jin, Dong-Gyu (Department of Pediatrics, Samsung Medical Center, Sungkyunkwan University School of Medicine)
- 박성원 (성균관 대학교 의과대학 소아과학교실) ;
- 손영배 (성균관 대학교 의과대학 소아과학교실) ;
- 김세화 (성균관 대학교 의과대학 소아과학교실) ;
- 조성윤 (성균관 대학교 의과대학 소아과학교실) ;
- 지선태 (성균관 대학교 의과대학 소아과학교실) ;
- 진동규 (성균관 대학교 의과대학 소아과학교실)
- Published : 2010.07.10
Abstract
Enzyme replacement of therapy (ERT) is one of the most promising therapeutic strategies for the treatment of lysosomal storage disorders. ERT is available in three types of Mucopolysaccharidosis (MPS): for MPS I (Aludrazyme